TABLE OF CONTENTS 1 INDUSTRY OVERVIEW 1.1 Friedreich Ataxia Drug Industry 1.1.1 Friedreich Ataxia Drug Overview 1.1.2 Terminology Definition in the Report 1.1.2.1 Capacity 1.1.2.2 Sales Volume 1.1.2.3 Sales Revenue 1.1.2.4 Ex-factory Price & Sales Price 1.1.2.5 Cost 1.1.2.6 Gross Margin 1.2 Products & Services Overview Scope 1.3 Friedreich Ataxia Drug in the Industry Chain 1.4 Industry Dynamics & Regulations 1.5 Global Market Overview 2 UPSTREAM & MANUFACTURING 2.1 Raw Materials / Components 2.2 Procurement Methods & Channels 2.3 Cost Structure & Manufacturing 2.4 Industry Capacity Overview 2.5 Production Distribution by Geography 2.5.1 Production in Major Regions / Countries 2.5.2 Trade Flow Overview 3 PRODUCT SEGMENT 3.1 Product Segmentation Market (2017 to 2021E) 3.1.1 ADVM-063 Market 3.1.2 AGIL-FA Market 3.1.3 BHV-4157 Market 3.1.4 BVA-202 Market 3.1.5 Others Market 3.2 Market Status 4 APPLICATION / END-USE SEGMENT 4.1 Application Segmentation Market (2016 to 2021E) 4.1.1 Clinic Market 4.1.2 Hospital Market 4.1.3 Others Market 4.2 Market Status 5 NORTH AMERICA 5.1 North America Market Growth 5.2 North America Market by Countries 5.3 Major Countries Market Growth 5.3.1 United States Market Size and Growth (2016-2021E) 5.3.2 Canada Market Size and Growth (2016-2021E) 5.3.3 Mexico Market Size and Growth (2016-2021E) 6 EUROPE 6.1 Europe Market Growth 6.2 Europe Market by Countries 6.3 Major Countries Market Growth 6.3.1 Germany Market Size and Growth (2016-2021E) 6.3.2 UK Market Size and Growth (2016-2021E) 6.3.3 France Market Size and Growth (2016-2021E) 6.3.4 Russia Market Size and Growth (2016-2021E) 6.3.5 Italy Market Size and Growth (2016-2021E) 6.3.6 Rest of Europe Market Size and Growth (2016-2021E) 7 ASIA-PACIFIC 7.1 ASIA-PACIFIC Market Growth 7.2 ASIA-PACIFIC Market by Countries 7.3 Major Countries Market Growth 7.3.1 China Market Size and Growth (2016-2021E) 7.3.2 India Market Size and Growth (2016-2021E) 7.3.3 Japan Market Size and Growth (2016-2021E) 7.3.4 South Korea Market Size and Growth (2016-2021E) 7.3.5 Southeast Asia Market Size and Growth (2016-2021E) 7.3.6 Australia Market Size and Growth (2016-2021E) 7.3.7 Rest of Asia Pacific Market Size and Growth (2016-2021E) 8 SOUTH AMERICA 8.1 South America Market Growth 8.2 South America Market by Countries 8.3 Major Countries Market Growth 8.3.1 Brazil Market Size and Growth (2016-2021E) 8.3.2 Argentina Market Size and Growth (2016-2021E) 8.3.3 Rest of South America Market Size and Growth (2016-2021E) 9 MIDDLE EAST & AFRICA 9.1 Middle East and Africa Market Growth 9.2 Middle East and Africa Market by Countries 9.3 Major Countries Market Growth 9.3.1 GCC Market Size and Growth (2016-2021E) 9.3.2 North Africa Market Size and Growth (2016-2021E) 9.3.3 South Africa Market Size and Growth (2016-2021E) 9.3.4 Rest of Middle East & Africa Market Size and Growth (2016-2021E) 10 MARKET FORECAST 10.1 Global Market Forecast Overview 10.2 Global Market Forecast by Type 10.3 Global Market Forecast by Application / End-Use 10.4 Global Market Forecast by Region 11 COMPETITION OF MAJOR PLAYERS 11.1 Adverum Biotechnologies Inc (Company Profile, Products Overview, Sales Data, Latest Developments etc.) 11.1.1 Adverum Biotechnologies Inc Profile 11.1.2 Adverum Biotechnologies Inc Products & Services Overview 11.1.3 Adverum Biotechnologies Inc Main Business 11.1.4 Adverum Biotechnologies Inc Business Operation 11.2 BioMarin Pharmaceutical Inc. (Company Profile, Products Overview, Sales Data, Latest Developments etc.) 11.2.1 BioMarin Pharmaceutical Inc. Profile 11.2.2 BioMarin Pharmaceutical Inc. Products & Services 11.2.3 BioMarin Pharmaceutical Inc. Main Business 11.2.4 BioMarin Pharmaceutical Inc. Business Operation 11.3 Biovista Inc. (Company Profile, Products Overview, Sales Data, Latest Developments etc.) 11.3.1 Biovista Inc. Profile 11.3.2 Biovista Inc. Products & Services 11.3.3 Biovista Inc. Main Business 11.3.4 Biovista Inc. Business Operation 11.4 Cardero Therapeutics Inc (Company Profile, Products Overview, Sales Data, Latest Developments etc.) 11.4.1 Cardero Therapeutics Inc Profile 11.4.2 Cardero Therapeutics Inc Products & Services 11.4.3 Cardero Therapeutics Inc Main Business 11.4.4 Cardero Therapeutics Inc Business Operation 11.5 Catabasis Pharmaceuticals, Inc. (Company Profile, Products Overview, Sales Data, Latest Developments etc.) 11.5.1 Catabasis Pharmaceuticals, Inc. Profile 11.5.2 Catabasis Pharmaceuticals, Inc. Products & Services 11.5.3 Catabasis Pharmaceuticals, Inc. Main Business 11.5.4 Catabasis Pharmaceuticals, Inc. Business Operation 11.6 Forward Pharma A/S (Company Profile, Products Overview, Sales Data, Latest Developments etc.) 11.6.1 Forward Pharma A/S Profile 11.6.2 Forward Pharma A/S Products & Services 11.6.3 Forward Pharma A/S Main Business 11.6.4 Forward Pharma A/S Business Operation 11.7 Ixchel Pharma LLC (Company Profile, Products Overview, Sales Data, Latest Developments etc.) 11.7.1 Ixchel Pharma LLC Profile 11.7.2 Ixchel Pharma LLC Products & Services 11.7.3 Ixchel Pharma LLC Main Business 11.7.4 Ixchel Pharma LLC Business Operation 11.8 Pfizer Inc (Company Profile, Products Overview, Sales Data, Latest Developments etc.) 11.8.1 Pfizer Inc Profile 11.8.2 Pfizer Inc Products & Services 11.8.3 Pfizer Inc Main Business 11.8.4 Pfizer Inc Business Operation 11.9 ProQR Therapeutics NV (Company Profile, Products Overview, Sales Data, Latest Developments etc.) 11.9.1 ProQR Therapeutics NV Profile 11.9.2 ProQR Therapeutics NV Products & Services 11.9.3 ProQR Therapeutics NV Main Business 11.9.4 ProQR Therapeutics NV Business Operation 11.10 RaNA Therapeutics Inc (Company Profile, Products Overview, Sales Data, Latest Developments etc.) 11.10.1 RaNA Therapeutics Inc Profile 11.10.2 RaNA Therapeutics Inc Products & Services 11.10.3 RaNA Therapeutics Inc Main Business 11.10.4 RaNA Therapeutics Inc Business Operation 11.11 Reata Pharmaceuticals Inc (Company Profile, Products Overview, Sales Data, Latest Developments etc.) 11.11.1 Reata Pharmaceuticals Inc Profile 11.11.2 Reata Pharmaceuticals Inc Products & Services 11.11.3 Reata Pharmaceuticals Inc Main Business 11.11.4 Reata Pharmaceuticals Inc Business Operation 11.12 Retrotope Inc (Company Profile, Products Overview, Sales Data, Latest Developments etc.) 11.12.1 Retrotope Inc Profile 11.12.2 Retrotope Inc Products & Services 11.12.3 Retrotope Inc Main Business 11.12.4 Retrotope Inc Business Operation 11.13 Shire Plc (Company Profile, Products Overview, Sales Data, Latest Developments etc.) 11.13.1 Shire Plc Profile 11.13.2 Shire Plc Products & Services 11.13.3 Shire Plc Main Business 11.13.4 Shire Plc Business Operation 11.14 STATegics Inc (Company Profile, Products Overview, Sales Data, Latest Developments etc.) 11.14.1 STATegics Inc Profile 11.14.2 STATegics Inc Products & Services 11.14.3 STATegics Inc Main Business 11.14.4 STATegics Inc Business Operation 11.15 Voyager Therapeutics Inc (Company Profile, Products Overview, Sales Data, Latest Developments etc.) 11.15.1 Voyager Therapeutics Inc Profile 11.15.2 Voyager Therapeutics Inc Products & Services 11.15.3 Voyager Therapeutics Inc Main Business 11.15.4 Voyager Therapeutics Inc Business Operation 12 COMPANY COMPETITION 12.1 Global Sales by Company 12.1.1 Global Sales by Company 12.1.2 Global Sales Share by Company 12.2 Price & Gross Margin 12.3 Landscape of Major Companies in the Market 12.3.1 Major Companies Product Type List 12.3.1 Manufacturing Regions and Headquarters of Major Companies 12.3.1 Mergers & Acquisitions 12.4 Competitive Environment for New Entrants 12.4.1 Michael Porter's Five Forces Model 12.4.2 SWOT 13 ENVIRONMENT OVERVIEW 13.1 Impact of COVID-19 13.2 Geopolitics Overview 13.3 Economic Overview of Major Countries 14 RESEARCH CONCLUSION

LIST OF TABLE TABLE ~ Friedreich Ataxia Drug Industry Dynamics & Regulations List TABLE ~ Global Friedreich Ataxia Drug Sales Volume, Revenue, Price, Cost and Margin, 2016-2021E TABLE ~ ADVM-063 Market Size (USD Million & Volume), Pric (USD/Volume) 2016-2021E TABLE ~ ADVM-063 Market Size (Volume) 2016-2021E and Year-over-year (YOY) Growth (%) 2017-2021E TABLE ~ AGIL-FA Market Size (USD Million & Volume), Pric (USD/Volume) 2016-2021E TABLE ~ AGIL-FA Market Size (Volume) 2016-2021E and Year-over-year (YOY) Growth (%) 2017-2021E TABLE ~ BHV-4157 Market Size (USD Million & Volume), Pric (USD/Volume) 2016-2021E TABLE ~ BHV-4157 Market Size (Volume) 2016-2021E and Year-over-year (YOY) Growth (%) 2017-2021E TABLE ~ BVA-202 Market Size (USD Million & Volume), Pric (USD/Volume) 2016-2021E TABLE ~ BVA-202 Market Size (Volume) 2016-2021E and Year-over-year (YOY) Growth (%) 2017-2021E TABLE ~ Others Market Size (USD Million & Volume), Pric (USD/Volume) 2016-2021E TABLE ~ Others Market Size (Volume) 2016-2021E and Year-over-year (YOY) Growth (%) 2017-2021E TABLE ~ Global Friedreich Ataxia Drug Market Size by Type, 2016-2021E, in USD Million TABLE ~ Global Friedreich Ataxia Drug Market Size by Type, 2016-2021E, in Volume TABLE ~ Clinic Market Size (USD Million & Volume), Pric (USD/Volume) 2016-2021E TABLE ~ Clinic Market Size (Volume) 2016-2021E and Year-over-year (YOY) Growth (%) 2017-2021E TABLE ~ Hospital Market Size (USD Million & Volume), Pric (USD/Volume) 2016-2021E TABLE ~ Hospital Market Size (Volume) 2016-2021E and Year-over-year (YOY) Growth (%) 2017-2021E TABLE ~ Others Market Size (USD Million & Volume), Pric (USD/Volume) 2016-2021E TABLE ~ Others Market Size (Volume) 2016-2021E and Year-over-year (YOY) Growth (%) 2017-2021E TABLE ~ Global Friedreich Ataxia Drug Market Size by Type, 2016-2021E, in USD Million TABLE ~ Global Friedreich Ataxia Drug Market Size by Type, 2016-2021E, in Volume TABLE ~ North America Friedreich Ataxia Drug Sales by Countries 2016-2021E, in USD Million TABLE ~ North America Friedreich Ataxia Drug Sales Share by Countries 2016-2021E, in USD Million TABLE ~ North America Friedreich Ataxia Drug Sales by Countries 2016-2021E, in Volume TABLE ~ North America Friedreich Ataxia Drug Sales Share by Countries 2016-2021E, in Volume TABLE ~ United States Market Size (USD Million & Volume), Pric (USD/Volume) 2016-2021E TABLE ~ Canada Market Size (USD Million & Volume), Pric (USD/Volume) 2016-2021E TABLE ~ Mexico Market Size (USD Million & Volume), Pric (USD/Volume) 2016-2021E TABLE ~ Europe Friedreich Ataxia Drug Sales by Countries 2016-2021E, in USD Million TABLE ~ Europe Friedreich Ataxia Drug Sales Share by Countries 2016-2021E, in USD Million TABLE ~ Europe Friedreich Ataxia Drug Sales by Countries 2016-2021E, in Volume TABLE ~ Europe Friedreich Ataxia Drug Sales Share by Countries 2016-2021E, in Volume TABLE ~ Germany Market Size (USD Million & Volume), Pric (USD/Volume) 2016-2021E TABLE ~ UK Market Size (USD Million & Volume), Pric (USD/Volume) 2016-2021E TABLE ~ France Market Size (USD Million & Volume), Pric (USD/Volume) 2016-2021E TABLE ~ Russia Market Size (USD Million & Volume), Pric (USD/Volume) 2016-2021E TABLE ~ Italy Market Size (USD Million & Volume), Pric (USD/Volume) 2016-2021E TABLE ~ Rest of Europe Market Size (USD Million & Volume), Pric (USD/Volume) 2016-2021E TABLE ~ ASIA-PACIFIC Friedreich Ataxia Drug Sales by Countries 2016-2021E, in USD Million TABLE ~ ASIA-PACIFIC Friedreich Ataxia Drug Sales Share by Countries 2016-2021E, in USD Million TABLE ~ ASIA-PACIFIC Friedreich Ataxia Drug Sales by Countries 2016-2021E, in Volume TABLE ~ ASIA-PACIFIC Friedreich Ataxia Drug Sales Share by Countries 2016-2021E, in Volume TABLE ~ China Market Size (USD Million & Volume), Pric (USD/Volume) 2016-2021E TABLE ~ India Market Size (USD Million & Volume), Pric (USD/Volume) 2016-2021E TABLE ~ Japan Market Size (USD Million & Volume), Pric (USD/Volume) 2016-2021E TABLE ~ South Korea Market Size (USD Million & Volume), Pric (USD/Volume) 2016-2021E TABLE ~ Southeast Asia Market Size (USD Million & Volume), Pric (USD/Volume) 2016-2021E TABLE ~ Australia Market Size (USD Million & Volume), Pric (USD/Volume) 2016-2021E TABLE ~ Rest of Asia Pacific Market Size (USD Million & Volume), Pric (USD/Volume) 2016-2021E TABLE ~ South America Friedreich Ataxia Drug Sales by Countries 2016-2021E, in USD Million TABLE ~ South America Friedreich Ataxia Drug Sales Share by Countries 2016-2021E, in USD Million TABLE ~ South America Friedreich Ataxia Drug Sales by Countries 2016-2021E, in Volume TABLE ~ South America Friedreich Ataxia Drug Sales Share by Countries 2016-2021E, in Volume TABLE ~ Brazil Market Size (USD Million & Volume), Pric (USD/Volume) 2016-2021E TABLE ~ Argentina Market Size (USD Million & Volume), Pric (USD/Volume) 2016-2021E TABLE ~ Rest of South America Market Size (USD Million & Volume), Pric (USD/Volume) 2016-2021E TABLE ~ Middle East and Africa Friedreich Ataxia Drug Sales by Countries 2016-2021E, in USD Million TABLE ~ Middle East and Africa Friedreich Ataxia Drug Sales Share by Countries 2016-2021E, in USD Million TABLE ~ Middle East and Africa Friedreich Ataxia Drug Sales by Countries 2016-2021E, in Volume TABLE ~ Middle East and Africa Friedreich Ataxia Drug Sales Share by Countries 2016-2021E, in Volume TABLE ~ GCC Market Size (USD Million & Volume), Pric (USD/Volume) 2016-2021E TABLE ~ North Africa Market Size (USD Million & Volume), Pric (USD/Volume) 2016-2021E TABLE ~ South Africa Market Size (USD Million & Volume), Pric (USD/Volume) 2016-2021E TABLE ~ Rest of Middle East & Africa Market Size (USD Million & Volume), Pric (USD/Volume) 2016-2021E TABLE ~ Global Friedreich Ataxia Drug Sales Forecast by Type 2022F-2026F, in USD Million TABLE ~ Global Friedreich Ataxia Drug Sales Share Forecast by Type 2022F-2026F, in USD Million TABLE ~ Global Friedreich Ataxia Drug Sales Forecast by Type 2022F-2026F, in Volume TABLE ~ Global Friedreich Ataxia Drug Sales Share Forecast by Type 2022F-2026F, in Volume TABLE ~ Global Friedreich Ataxia Drug Sales Forecast by Application / End-Use 2022F-2026F, in USD Million TABLE ~ Global Friedreich Ataxia Drug Sales Share Forecast by Application / End-Use 2022F-2026F, in USD Million TABLE ~ Global Friedreich Ataxia Drug Sales Forecast by Application / End-Use 2022F-2026F, in Volume TABLE ~ Global Friedreich Ataxia Drug Sales Share Forecast by Application / End-Use 2022F-2026F, in Volume TABLE ~ Global Friedreich Ataxia Drug Sales Forecast by Region 2022F-2026F, in USD Million TABLE ~ Global Friedreich Ataxia Drug Sales Share Forecast by Region 2022F-2026F, in USD Million TABLE ~ Global Friedreich Ataxia Drug Sales Forecast by Region 2022F-2026F, in Volume TABLE ~ Global Friedreich Ataxia Drug Sales Share Forecast by Region 2022F-2026F, in Volume TABLE ~ Adverum Biotechnologies Inc Overview List TABLE ~ Products & Services List of Adverum Biotechnologies Inc TABLE ~ Business Operation of Adverum Biotechnologies Inc (Sales Revenue, Sales Volume, Price, Cost, Gross Margin) TABLE ~ BioMarin Pharmaceutical Inc. Overview List TABLE ~ Products & Services List of BioMarin Pharmaceutical Inc. TABLE ~ Business Operation of BioMarin Pharmaceutical Inc. (Sales Revenue, Sales Volume, Price, Cost, Gross Margin) TABLE ~ Biovista Inc. Overview List TABLE ~ Products & Services List of Biovista Inc. TABLE ~ Business Operation of Biovista Inc. (Sales Revenue, Sales Volume, Price, Cost, Gross Margin) TABLE ~ Cardero Therapeutics Inc Overview List TABLE ~ Products & Services List of Cardero Therapeutics Inc TABLE ~ Business Operation of Cardero Therapeutics Inc (Sales Revenue, Sales Volume, Price, Cost, Gross Margin) TABLE ~ Catabasis Pharmaceuticals, Inc. Overview List TABLE ~ Products & Services List of Catabasis Pharmaceuticals, Inc. TABLE ~ Business Operation of Catabasis Pharmaceuticals, Inc. (Sales Revenue, Sales Volume, Price, Cost, Gross Margin) TABLE ~ Forward Pharma A/S Overview List TABLE ~ Products & Services List of Forward Pharma A/S TABLE ~ Business Operation of Forward Pharma A/S (Sales Revenue, Sales Volume, Price, Cost, Gross Margin) TABLE ~ Ixchel Pharma LLC Overview List TABLE ~ Products & Services List of Ixchel Pharma LLC TABLE ~ Business Operation of Ixchel Pharma LLC (Sales Revenue, Sales Volume, Price, Cost, Gross Margin) TABLE ~ Pfizer Inc Overview List TABLE ~ Products & Services List of Pfizer Inc TABLE ~ Business Operation of Pfizer Inc (Sales Revenue, Sales Volume, Price, Cost, Gross Margin) TABLE ~ ProQR Therapeutics NV Overview List TABLE ~ Products & Services List of ProQR Therapeutics NV TABLE ~ Business Operation of ProQR Therapeutics NV (Sales Revenue, Sales Volume, Price, Cost, Gross Margin) TABLE ~ RaNA Therapeutics Inc Overview List TABLE ~ Products & Services List of RaNA Therapeutics Inc TABLE ~ Business Operation of RaNA Therapeutics Inc (Sales Revenue, Sales Volume, Price, Cost, Gross Margin) TABLE ~ Reata Pharmaceuticals Inc Overview List TABLE ~ Products & Services List of Reata Pharmaceuticals Inc TABLE ~ Business Operation of Reata Pharmaceuticals Inc (Sales Revenue, Sales Volume, Price, Cost, Gross Margin) TABLE ~ Retrotope Inc Overview List TABLE ~ Products & Services List of Retrotope Inc TABLE ~ Business Operation of Retrotope Inc (Sales Revenue, Cost, Gross Margin) TABLE ~ Shire Plc Overview List TABLE ~ Products & Services List of Shire Plc TABLE ~ Business Operation of Shire Plc (Sales Revenue, Sales Volume, Price, Cost, Gross Margin) TABLE ~ STATegics Inc Overview List TABLE ~ Products & Services List of STATegics Inc TABLE ~ Business Operation of STATegics Inc (Sales Revenue, Cost, Gross Margin) TABLE ~ Voyager Therapeutics Inc Overview List TABLE ~ Products & Services List of Voyager Therapeutics Inc TABLE ~ Business Operation of Voyager Therapeutics Inc (Sales Revenue, Cost, Gross Margin) TABLE ~ Global Friedreich Ataxia Drug Sales by Company 2016-2021E, in USD Million TABLE ~ Global Friedreich Ataxia Drug Sales by Company 2016-2021E, in Volume TABLE ~ Global Friedreich Ataxia Drug Sales Share by Company 2016-2021E, in USD Million TABLE ~ Global Friedreich Ataxia Drug Sales Share by Company 2016-2021E, in Volume TABLE ~ Global Friedreich Ataxia Drug Sales Price by Company 2016-2021E, in USD/Volume TABLE ~ Global Friedreich Ataxia Drug Gross Margin by Company 2016-2021E TABLE ~ Major Companies Product Type List TABLE ~ Major Companies Product Type List TABLE ~ Mergers & Acquisitions in the Market