1 Report Overview 1.1 Study Scope 1.2 Market Analysis by Type 1.2.1 Global Pompe Disease Treatment Market Size Growth Rate by Type: 2017 VS 2021 VS 2028 1.2.2 Infantile-Onset Pompe Disease 1.2.3 Adult-Onset Pompe Disease 1.3 Market by Application 1.3.1 Global Pompe Disease Treatment Market Share by Application: 2017 VS 2021 VS 2028 1.3.2 Hospital 1.3.3 Medical Center 1.3.4 Other 1.4 Study Objectives 1.5 Years Considered 2 Global Growth Trends 2.1 Global Pompe Disease Treatment Market Perspective (2017-2028) 2.2 Pompe Disease Treatment Growth Trends by Region 2.2.1 Pompe Disease Treatment Market Size by Region: 2017 VS 2021 VS 2028 2.2.2 Pompe Disease Treatment Historic Market Size by Region (2017-2022) 2.2.3 Pompe Disease Treatment Forecasted Market Size by Region (2023-2028) 2.3 Pompe Disease Treatment Market Dynamics 2.3.1 Pompe Disease Treatment Industry Trends 2.3.2 Pompe Disease Treatment Market Drivers 2.3.3 Pompe Disease Treatment Market Challenges 2.3.4 Pompe Disease Treatment Market Restraints 3 Competition Landscape by Key Players 3.1 Global Top Pompe Disease Treatment Players by Revenue 3.1.1 Global Top Pompe Disease Treatment Players by Revenue (2017-2022) 3.1.2 Global Pompe Disease Treatment Revenue Market Share by Players (2017-2022) 3.2 Global Pompe Disease Treatment Market Share by Company Type (Tier 1, Tier 2, and Tier 3) 3.3 Players Covered: Ranking by Pompe Disease Treatment Revenue 3.4 Global Pompe Disease Treatment Market Concentration Ratio 3.4.1 Global Pompe Disease Treatment Market Concentration Ratio (CR5 and HHI) 3.4.2 Global Top 10 and Top 5 Companies by Pompe Disease Treatment Revenue in 2021 3.5 Pompe Disease Treatment Key Players Head office and Area Served 3.6 Key Players Pompe Disease Treatment Product Solution and Service 3.7 Date of Enter into Pompe Disease Treatment Market 3.8 Mergers & Acquisitions, Expansion Plans 4 Pompe Disease Treatment Breakdown Data by Type 4.1 Global Pompe Disease Treatment Historic Market Size by Type (2017-2022) 4.2 Global Pompe Disease Treatment Forecasted Market Size by Type (2023-2028) 5 Pompe Disease Treatment Breakdown Data by Application 5.1 Global Pompe Disease Treatment Historic Market Size by Application (2017-2022) 5.2 Global Pompe Disease Treatment Forecasted Market Size by Application (2023-2028) 6 North America 6.1 North America Pompe Disease Treatment Market Size (2017-2028) 6.2 North America Pompe Disease Treatment Market Size by Country (2017-2022) 6.3 North America Pompe Disease Treatment Market Size by Country (2023-2028) 6.4 United States 6.5 Canada 7 Europe 7.1 Europe Pompe Disease Treatment Market Size (2017-2028) 7.2 Europe Pompe Disease Treatment Market Size by Country (2017-2022) 7.3 Europe Pompe Disease Treatment Market Size by Country (2023-2028) 7.4 Germany 7.5 France 7.6 U.K. 7.7 Italy 7.8 Russia 7.9 Nordic Countries 8 Asia-Pacific 8.1 Asia-Pacific Pompe Disease Treatment Market Size (2017-2028) 8.2 Asia-Pacific Pompe Disease Treatment Market Size by Country (2017-2022) 8.3 Asia-Pacific Pompe Disease Treatment Market Size by Country (2023-2028) 8.4 China 8.5 Japan 8.6 South Korea 8.7 Southeast Asia 8.8 India 8.9 Australia 9 Latin America 9.1 Latin America Pompe Disease Treatment Market Size (2017-2028) 9.2 Latin America Pompe Disease Treatment Market Size by Country (2017-2022) 9.3 Latin America Pompe Disease Treatment Market Size by Country (2023-2028) 9.4 Mexico 9.5 Brazil 10 Middle East & Africa 10.1 Middle East & Africa Pompe Disease Treatment Market Size (2017-2028) 10.2 Middle East & Africa Pompe Disease Treatment Market Size by Country (2017-2022) 10.3 Middle East & Africa Pompe Disease Treatment Market Size by Country (2023-2028) 10.4 Turkey 10.5 Saudi Arabia 10.6 UAE 11 Key Players Profiles 11.1 Amicus Therapeutics 11.1.1 Amicus Therapeutics Company Detail 11.1.2 Amicus Therapeutics Business Overview 11.1.3 Amicus Therapeutics Pompe Disease Treatment Introduction 11.1.4 Amicus Therapeutics Revenue in Pompe Disease Treatment Business (2017-2022) 11.1.5 Amicus Therapeutics Recent Development 11.2 Audentes Therapeutics 11.2.1 Audentes Therapeutics Company Detail 11.2.2 Audentes Therapeutics Business Overview 11.2.3 Audentes Therapeutics Pompe Disease Treatment Introduction 11.2.4 Audentes Therapeutics Revenue in Pompe Disease Treatment Business (2017-2022) 11.2.5 Audentes Therapeutics Recent Development 11.3 Sanofi Genzyme 11.3.1 Sanofi Genzyme Company Detail 11.3.2 Sanofi Genzyme Business Overview 11.3.3 Sanofi Genzyme Pompe Disease Treatment Introduction 11.3.4 Sanofi Genzyme Revenue in Pompe Disease Treatment Business (2017-2022) 11.3.5 Sanofi Genzyme Recent Development 11.4 EpiVax 11.4.1 EpiVax Company Detail 11.4.2 EpiVax Business Overview 11.4.3 EpiVax Pompe Disease Treatment Introduction 11.4.4 EpiVax Revenue in Pompe Disease Treatment Business (2017-2022) 11.4.5 EpiVax Recent Development 11.5 Oxyrane 11.5.1 Oxyrane Company Detail 11.5.2 Oxyrane Business Overview 11.5.3 Oxyrane Pompe Disease Treatment Introduction 11.5.4 Oxyrane Revenue in Pompe Disease Treatment Business (2017-2022) 11.5.5 Oxyrane Recent Development 11.6 Sangamo BioSciences 11.6.1 Sangamo BioSciences Company Detail 11.6.2 Sangamo BioSciences Business Overview 11.6.3 Sangamo BioSciences Pompe Disease Treatment Introduction 11.6.4 Sangamo BioSciences Revenue in Pompe Disease Treatment Business (2017-2022) 11.6.5 Sangamo BioSciences Recent Development 11.7 Valerion Therapeutics 11.7.1 Valerion Therapeutics Company Detail 11.7.2 Valerion Therapeutics Business Overview 11.7.3 Valerion Therapeutics Pompe Disease Treatment Introduction 11.7.4 Valerion Therapeutics Revenue in Pompe Disease Treatment Business (2017-2022) 11.7.5 Valerion Therapeutics Recent Development 12 Analyst's Viewpoints/Conclusions 13 Appendix 13.1 Research Methodology 13.1.1 Methodology/Research Approach 13.1.2 Data Source 13.2 Disclaimer 13.3 Author Details

List of Tables Table 1. Global Pompe Disease Treatment Market Size Growth Rate by Type (US$ Million): 2017 VS 2021 VS 2028 Table 2. Key Players of Infantile-Onset Pompe Disease Table 3. Key Players of Adult-Onset Pompe Disease Table 4. Global Pompe Disease Treatment Market Size Growth by Application (US$ Million): 2017 VS 2021 VS 2028 Table 5. Global Pompe Disease Treatment Market Size by Region (US$ Million): 2017 VS 2021 VS 2028 Table 6. Global Pompe Disease Treatment Market Size by Region (2017-2022) & (US$ Million) Table 7. Global Pompe Disease Treatment Market Share by Region (2017-2022) Table 8. Global Pompe Disease Treatment Forecasted Market Size by Region (2023-2028) & (US$ Million) Table 9. Global Pompe Disease Treatment Market Share by Region (2023-2028) Table 10. Pompe Disease Treatment Market Trends Table 11. Pompe Disease Treatment Market Drivers Table 12. Pompe Disease Treatment Market Challenges Table 13. Pompe Disease Treatment Market Restraints Table 14. Global Pompe Disease Treatment Revenue by Players (2017-2022) & (US$ Million) Table 15. Global Pompe Disease Treatment Market Share by Players (2017-2022) Table 16. Global Top Pompe Disease Treatment Players by Company Type (Tier 1, Tier 2, and Tier 3) & (based on the Revenue in Pompe Disease Treatment as of 2021) Table 17. Ranking of Global Top Pompe Disease Treatment Companies by Revenue (US$ Million) in 2021 Table 18. Global 5 Largest Players Market Share by Pompe Disease Treatment Revenue (CR5 and HHI) & (2017-2022) Table 19. Key Players Headquarters and Area Served Table 20. Key Players Pompe Disease Treatment Product Solution and Service Table 21. Date of Enter into Pompe Disease Treatment Market Table 22. Mergers & Acquisitions, Expansion Plans Table 23. Global Pompe Disease Treatment Market Size by Type (2017-2022) & (US$ Million) Table 24. Global Pompe Disease Treatment Revenue Market Share by Type (2017-2022) Table 25. Global Pompe Disease Treatment Forecasted Market Size by Type (2023-2028) & (US$ Million) Table 26. Global Pompe Disease Treatment Revenue Market Share by Type (2023-2028) Table 27. Global Pompe Disease Treatment Market Size by Application (2017-2022) & (US$ Million) Table 28. Global Pompe Disease Treatment Revenue Market Share by Application (2017-2022) Table 29. Global Pompe Disease Treatment Forecasted Market Size by Application (2023-2028) & (US$ Million) Table 30. Global Pompe Disease Treatment Revenue Market Share by Application (2023-2028) Table 31. North America Pompe Disease Treatment Market Size by Country (2017-2022) & (US$ Million) Table 32. North America Pompe Disease Treatment Market Size by Country (2023-2028) & (US$ Million) Table 33. Europe Pompe Disease Treatment Market Size by Country (2017-2022) & (US$ Million) Table 34. Europe Pompe Disease Treatment Market Size by Country (2023-2028) & (US$ Million) Table 35. Asia-Pacific Pompe Disease Treatment Market Size by Region (2017-2022) & (US$ Million) Table 36. Asia-Pacific Pompe Disease Treatment Market Size by Region (2023-2028) & (US$ Million) Table 37. Latin America Pompe Disease Treatment Market Size by Country (2017-2022) & (US$ Million) Table 38. Latin America Pompe Disease Treatment Market Size by Country (2023-2028) & (US$ Million) Table 39. Middle East & Africa Pompe Disease Treatment Market Size by Country (2017-2022) & (US$ Million) Table 40. Middle East & Africa Pompe Disease Treatment Market Size by Country (2023-2028) & (US$ Million) Table 41. Amicus Therapeutics Company Detail Table 42. Amicus Therapeutics Business Overview Table 43. Amicus Therapeutics Pompe Disease Treatment Product Table 44. Amicus Therapeutics Revenue in Pompe Disease Treatment Business (2017-2022) & (US$ Million) Table 45. Amicus Therapeutics Recent Development Table 46. Audentes Therapeutics Company Detail Table 47. Audentes Therapeutics Business Overview Table 48. Audentes Therapeutics Pompe Disease Treatment Product Table 49. Audentes Therapeutics Revenue in Pompe Disease Treatment Business (2017-2022) & (US$ Million) Table 50. Audentes Therapeutics Recent Development Table 51. Sanofi Genzyme Company Detail Table 52. Sanofi Genzyme Business Overview Table 53. Sanofi Genzyme Pompe Disease Treatment Product Table 54. Sanofi Genzyme Revenue in Pompe Disease Treatment Business (2017-2022) & (US$ Million) Table 55. Sanofi Genzyme Recent Development Table 56. EpiVax Company Detail Table 57. EpiVax Business Overview Table 58. EpiVax Pompe Disease Treatment Product Table 59. EpiVax Revenue in Pompe Disease Treatment Business (2017-2022) & (US$ Million) Table 60. EpiVax Recent Development Table 61. Oxyrane Company Detail Table 62. Oxyrane Business Overview Table 63. Oxyrane Pompe Disease Treatment Product Table 64. Oxyrane Revenue in Pompe Disease Treatment Business (2017-2022) & (US$ Million) Table 65. Oxyrane Recent Development Table 66. Sangamo BioSciences Company Detail Table 67. Sangamo BioSciences Business Overview Table 68. Sangamo BioSciences Pompe Disease Treatment Product Table 69. Sangamo BioSciences Revenue in Pompe Disease Treatment Business (2017-2022) & (US$ Million) Table 70. Sangamo BioSciences Recent Development Table 71. Valerion Therapeutics Company Detail Table 72. Valerion Therapeutics Business Overview Table 73. Valerion Therapeutics Pompe Disease Treatment Product Table 74. Valerion Therapeutics Revenue in Pompe Disease Treatment Business (2017-2022) & (US$ Million) Table 75. Valerion Therapeutics Recent Development Table 76. Research Programs/Design for This Report Table 77. Key Data Information from Secondary Sources Table 78. Key Data Information from Primary Sources List of Figures Figure 1. Global Pompe Disease Treatment Market Share by Type: 2021 VS 2028 Figure 2. Infantile-Onset Pompe Disease Features Figure 3. Adult-Onset Pompe Disease Features Figure 4. Global Pompe Disease Treatment Market Share by Application in 2021 & 2028 Figure 5. Hospital Case Studies Figure 6. Medical Center Case Studies Figure 7. Other Case Studies Figure 8. Pompe Disease Treatment Report Years Considered Figure 9. Global Pompe Disease Treatment Market Size (US$ Million), Year-over-Year: 2017-2028 Figure 10. Global Pompe Disease Treatment Market Size, (US$ Million), 2017 VS 2021 VS 2028 Figure 11. Global Pompe Disease Treatment Market Share by Region: 2021 VS 2028 Figure 12. Global Pompe Disease Treatment Market Share by Players in 2021 Figure 13. Global Top Pompe Disease Treatment Players by Company Type (Tier 1, Tier 2, and Tier 3) & (based on the Revenue in Pompe Disease Treatment as of 2021) Figure 14. The Top 10 and 5 Players Market Share by Pompe Disease Treatment Revenue in 2021 Figure 15. North America Pompe Disease Treatment Market Size YoY Growth (2017-2028) & (US$ Million) Figure 16. North America Pompe Disease Treatment Market Share by Country (2017-2028) Figure 17. United States Pompe Disease Treatment Market Size YoY Growth (2017-2028) & (US$ Million) Figure 18. Canada Pompe Disease Treatment Market Size YoY Growth (2017-2028) & (US$ Million) Figure 19. Europe Pompe Disease Treatment Market Size YoY Growth (2017-2028) & (US$ Million) Figure 20. Europe Pompe Disease Treatment Market Share by Country (2017-2028) Figure 21. Germany Pompe Disease Treatment Market Size YoY Growth (2017-2028) & (US$ Million) Figure 22. France Pompe Disease Treatment Market Size YoY Growth (2017-2028) & (US$ Million) Figure 23. U.K. Pompe Disease Treatment Market Size YoY Growth (2017-2028) & (US$ Million) Figure 24. Italy Pompe Disease Treatment Market Size YoY Growth (2017-2028) & (US$ Million) Figure 25. Russia Pompe Disease Treatment Market Size YoY Growth (2017-2028) & (US$ Million) Figure 26. Nordic Countries Pompe Disease Treatment Market Size YoY Growth (2017-2028) & (US$ Million) Figure 27. Asia-Pacific Pompe Disease Treatment Market Size YoY Growth (2017-2028) & (US$ Million) Figure 28. Asia-Pacific Pompe Disease Treatment Market Share by Region (2017-2028) Figure 29. China Pompe Disease Treatment Market Size YoY Growth (2017-2028) & (US$ Million) Figure 30. Japan Pompe Disease Treatment Market Size YoY Growth (2017-2028) & (US$ Million) Figure 31. South Korea Pompe Disease Treatment Market Size YoY Growth (2017-2028) & (US$ Million) Figure 32. Southeast Asia Pompe Disease Treatment Market Size YoY Growth (2017-2028) & (US$ Million) Figure 33. India Pompe Disease Treatment Market Size YoY Growth (2017-2028) & (US$ Million) Figure 34. Australia Pompe Disease Treatment Market Size YoY Growth (2017-2028) & (US$ Million) Figure 35. Latin America Pompe Disease Treatment Market Size YoY Growth (2017-2028) & (US$ Million) Figure 36. Latin America Pompe Disease Treatment Market Share by Country (2017-2028) Figure 37. Mexico Pompe Disease Treatment Market Size YoY Growth (2017-2028) & (US$ Million) Figure 38. Brazil Pompe Disease Treatment Market Size YoY Growth (2017-2028) & (US$ Million) Figure 39. Middle East & Africa Pompe Disease Treatment Market Size YoY Growth (2017-2028) & (US$ Million) Figure 40. Middle East & Africa Pompe Disease Treatment Market Share by Country (2017-2028) Figure 41. Turkey Pompe Disease Treatment Market Size YoY Growth (2017-2028) & (US$ Million) Figure 42. Saudi Arabia Pompe Disease Treatment Market Size YoY Growth (2017-2028) & (US$ Million) Figure 43. Amicus Therapeutics Revenue Growth Rate in Pompe Disease Treatment Business (2017-2022) Figure 44. Audentes Therapeutics Revenue Growth Rate in Pompe Disease Treatment Business (2017-2022) Figure 45. Sanofi Genzyme Revenue Growth Rate in Pompe Disease Treatment Business (2017-2022) Figure 46. EpiVax Revenue Growth Rate in Pompe Disease Treatment Business (2017-2022) Figure 47. Oxyrane Revenue Growth Rate in Pompe Disease Treatment Business (2017-2022) Figure 48. Sangamo BioSciences Revenue Growth Rate in Pompe Disease Treatment Business (2017-2022) Figure 49. Valerion Therapeutics Revenue Growth Rate in Pompe Disease Treatment Business (2017-2022) Figure 50. Bottom-up and Top-down Approaches for This Report Figure 51. Data Triangulation Figure 52. Key Executives Interviewed

Amicus Therapeutics Audentes Therapeutics Sanofi Genzyme EpiVax Oxyrane Sangamo BioSciences Valerion Therapeutics